Researchers at Kumamoto University have demonstrated that iron supplementation can significantly alleviate muscle pathology ...
An experimental RNA therapy from Avidity Biosciences has early clinical trial results showing it reduced by half the expression of a gene at the root of a rare, inherited form of muscular dystrophy ...
Researchers at Kumamoto University have demonstrated that iron supplementation can significantly alleviate muscle pathology and functional decline in a mouse model of facioscapulohumeral muscular ...
FSHD Society to host Avidity webinar on positive initial data from the Phase 1/2 FORTITUDE™ trial for people living with FSHD today at 1:00 p.m. ET "This World FSHD Day, we are excited to be joining ...
SAN DIEGO, April 22, 2020 (GLOBE NEWSWIRE) -- Bionano Genomics, Inc. (Nasdaq: BNGO) announced that the University of Iowa Hospitals and Clinics (UIHC) will switch their method of clinical molecular ...
Avidity Biosciences said Wednesday morning that an experimental medicine successfully knocked down the gene behind a form of muscular dystrophy being pursued by a fleet of drug companies. The ...
A 5K walk will be taking place this weekend in observance of a rare disease that many have never heard of. Joanne Dalessandro and her warriors will be in Barrington, Illinois, for the Chicagoland Walk ...
VANCOUVER, British Columbia--(BUSINESS WIRE)--SOLVE FSHD, a venture philanthropy organization dedicated to catalyzing innovation and overcoming barriers to accelerate new therapies for ...
Mark J. Christman continues to wait, but time is of the essence. Ongoing research and clinical trials are underway, but the U.S. Food and Drug Administration has not yet approved any treatments to ...
The investigational drug losmapimod did not significantly change expression of the gene behind facioscapulohumeral muscular dystrophy (FSHD), but it was associated with potential improvements in ...
Mark J. Christman doesn’t have the strength to hold his nearly 8-month-old grandson, William “Willie” Chavara. “I am weaker every year,” said Christman, who was diagnosed in 1977 with ...
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